Ophthalmology New Gene Therapy Found to be Safe for Eye Disease Retinitis PigmentosaJuly 23, 20240 Trial results presenting the safety and effectiveness of gene modifier therapy for treating retinitis pigmentosa associated with NR2E3 and RHO…
Neurology Research shows siRNA does not lower abnormal huntingtin gene levels in brain cells.July 23, 20240 New study highlights challenges in targeting mutant huntingtin mRNA in Huntington’s disease. A study on Huntington’s disease found that short…
Drug Discoveries New Advances in AAV8 Gene Therapy for Eye Conditions like Retinal DiseasesJuly 19, 20240 A recent study found that injections of adeno-associated virus 8 (AAV8) in the eye can trigger a proinflammatory T-cell immune…
